Galactosemia

Category: Endocrine & Metabolic / Disorders of Carbohydrate Metabolism

Galactosemia is a rare inherited metabolic disorder in which the body is unable to metabolize the sugar galactose, leading to its accumulation and causing severe damage to organs if untreated.

Global Prevalence

Estimated at 1 in 30,000 to 1 in 60,000 live births (source: National Organization for Rare Disorders).

Medical Breakthroughs

Discover the latest clinical trials and treatments for Galactosemia on JourneyForHealth.

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