Category: Genetic Disorders / Metabolic Disorders
Alpha-1 Antitrypsin Deficiency (AATD) is a genetic disorder that causes a deficiency of the alpha-1 antitrypsin protein, primarily leading to lung disease (emphysema) and liver disease.
Estimated 1 in 3,000 to 5,000 individuals of European descent, but often underdiagnosed. (Source: Alpha-1 Foundation)
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